Tolerance Adenoviridae/immunology Dynamin 2 AAV vector High-throughput sequencing Gait assessment Baculovirus Discriminant analysis AAV Adenoassociated viral vector Mice Antibodies/immunology/metabolism Insect cells Gene therapy Acute treatment CD8 + T lymphocytes Clinical trials Innate immunity Assembly-activating protein Centronuclear myopathy AUC Clinical trial Air tamponade DMD GC-content GRMD Immunosuppression Cerebellum Age Gene Transfer Infectivity Dose study Congenital amaurosis Accelerometry Capsid Human-monocyte-derived dendritic cells Gene-therapy AAV vectors Identity assay Homologous recombination Capsid thermal stability GRMD dog Bioorthogonality Cone photoreceptors Childhood blindness Animal model Immune response In vivo Homogeneity Duchenne Fluid-air exchange Animals Dystrophin Quality control Capsid thermostability Identity Exercise Manufacturing Immunogenicity inflammation gene therapy AAV Crigler–Najjar Syndrome Capsid assembly Eye surgery Gene Therapy Beta-subunit Ectopic expression Cell–virus interaction High-throughput technology Impurities Intrathymic gene transfer Homopolymers Immune responses Inflammation Genes CMC DMDmdx rat Engineering Intravitreal Skeletal muscle B-Lymphocytes/immunology/metabolism Cell therapy Inherited retinal dystrophies CNS Analytical ultracentrifugation Adeno-associated virus Antibody responses Intra-cerebrospinal fluid injection Bioconjugates Calcium Gene transfer Baculovirus expression vector Click chemistry Duchenne muscular dystrophy AAP Vector Treg ABCA4 Immunogenicity Humoral immunity Exon skipping Immunomodulation